A recent concert in Singapore was all about finding harmony through the talents that unite us in life, writes columnist.

For the second time, a person with DMD has died of acute liver failure after being treated with the one-time gene therapy Elevidys.

As her only son without DMD plays in a statewide all-star football game, columnist Betty Vertin reflects on his tie to his brothers.

Columnist Robin Stemple marks two anniversaries that forever altered his life. Despite the incredible challenges, he feels ...

The U.S. Food and Drug Administration (FDA) granted platform technology designation to the viral vector used in SRP-9003, an ...

The U.S. Food and Drug Administration (FDA) granted platform technology designation to the viral vector used in SRP-9003, an investigational gene therapy for limb ...

Patients are often the best experts on their disease, but what about emergency situations? Columnist Patrick Moeschen shares ...

Columnist Betty Vertin acknowledges the mixed feelings of fear and pride as her youngest son with DMD begins with high school band.

The U.S. Food and Drug Administration (FDA) has granted orphan drug status to ISX9-CPC, IPS Heart ’s experimental stem cell ...

Building empathy and having clear communication are key to improving patient outcomes in DMD, writes columnist.

An investigational gene therapy called GNT0004 has demonstrated sustained stabilization of motor function at up to two years of follow-up in two boys with Duchenne muscular dystrophy (DMD). The boys ...