A recent concert in Singapore was all about finding harmony through the talents that unite us in life, writes columnist.

For the second time, a person with DMD has died of acute liver failure after being treated with the one-time gene therapy Elevidys.

Patients are often the best experts on their disease, but what about emergency situations? Columnist Patrick Moeschen shares ...

Columnist Robin Stemple marks two anniversaries that forever altered his life. Despite the incredible challenges, he feels ...

The U.S. Food and Drug Administration (FDA) granted platform technology designation to the viral vector used in SRP-9003, an ...

Building empathy and having clear communication are key to improving patient outcomes in DMD, writes columnist.

As her only son without DMD plays in a statewide all-star football game, columnist Betty Vertin reflects on his tie to his brothers.

The U.S. Food and Drug Administration (FDA) has granted orphan drug status to ISX9-CPC, IPS Heart ’s experimental stem cell ...

Different types of muscular dystrophy (MD) may affect different muscle groups. Patients often have difficulty walking and may have problems with muscle control in other tasks, such as dressing or ...

Living with muscular dystrophy can be challenging, and there are considerations that must be taken into account on a day-to-basis and in certain situations to help patients manage the disease. Many ...

Duvyzat's approvals were based on the Phase 3 EPIDYS trial, which included 179 boys, ages 6 and older, who were able to walk.

Treatment with PF-06939926, an experimental gene therapy for Duchenne muscular dystrophy (DMD), was generally well-tolerated among ambulatory patients — boys able to walk — in a Phase 1B clinical ...